BioMarin将开始对PKU进行基因治疗的早期研究
根据当前的治疗指南，PKU患者需要终生控制自己的Phe水平,这需要终身治疗,BMN 307单剂量给药的成功开发应该是PKU治疗领域的重大突破。
BioM
糖PEG化-exei_Esperoct_糖PEG化-exei粉末预填充注射溶液antihemophilic说明书
[caption id="attachment_35888" align="alignleft" width="300"] Esperoct Kit 500IU/4mL（抗血友病因子[重组]，糖PEG化-exei粉末预
抗血友病因子[重组]聚乙二醇化_Adynovate_抗血友病因子[重组]聚乙二醇化冻干粉注射剂Antihemophilic说明书
[caption id="attachment_35929" align="alignleft" width="300"] Adynovate Intravenous Kit 2000IU（抗血友病因子[重组]聚乙二醇
![抗血友病因子[重组]聚乙二醇化_Adynovate_抗血友病因子[重组]聚乙二醇化冻干粉注射剂Antihemophilic说明书](https://www.yschn.com/wp-content/uploads/2020/07/1596082546-911c60d6e3414e9.gif)
抗血友病因子[重组]聚乙二醇化_Adynovate_抗血友病因子[重组]聚乙二醇化冻干粉注射剂Antihemophilic说明书
[caption id="attachment_35929" align="alignleft" width="300"] Adynovate Intravenous Kit 250IU（抗血友病因子[重组]聚乙二醇化
重组凝血因子XIII_NovoThirteen_重组凝血因子XIII冻干粉注射剂Catridecacog说明书
[caption id="attachment_35926" align="alignleft" width="300"] NovoThirteen kit 250units(重组凝血因子XIII冻干粉注射剂)[/capti
重组血友病因子_Veyvondi_重组血友病因子粉末注射溶液vonicog说明书
[caption id="attachment_35913" align="alignleft" width="300"] Veyvondi 1300IE(vonicog alfa 重组血友病因子粉末注射溶液)[/cap
重组血友病因子_Veyvondi_重组血友病因子粉末注射溶液vonicog说明书
[caption id="attachment_35913" align="alignleft" width="300"] Veyvondi 650IE(vonicog alfa 重组血友病因子粉末注射溶液)[/capt
![抗血友病因子[重组]猪序列_obizur_抗血友病因子[重组]猪序列冻干粉注射剂Antihemophilic中英对照说明书](https://www.yschn.com/wp-content/uploads/2020/07/1596081125-e32925b89807507.gif)
抗血友病因子[重组]猪序列_obizur_抗血友病因子[重组]猪序列冻干粉注射剂Antihemophilic中英对照说明书
[caption id="attachment_35906" align="alignleft" width="300"] obizur 500E Pulver(抗血友病因子[重组]猪序列冻干粉注射剂)[/capt
重组凝血因子IX_Refixia_重组凝血因子IX注射剂Nonacog说明书
[caption id="attachment_35888" align="alignleft" width="300"] Refixia 1000IU kit（Nonacog Beta Pegol 重组凝血因子IX注射剂
重组凝血因子IX_Refixia_重组凝血因子IX注射剂Nonacog说明书
[caption id="attachment_35888" align="alignleft" width="300"] Refixia 2000IU kit（Nonacog Beta Pegol 重组凝血因子IX注射剂
